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指定難病 — No.48

原発性抗リン脂質抗体症候群

検索語 Antiphospholipid Syndrome ・ 最終更新 2026-09-15 07:00 ・ 最新に更新

Data Sheet
指定 No.48
Src PubMed · CT.gov · jRCT

これは医療アドバイスではありません。診断・治療の判断は必ず主治医にご相談ください。論文や治験は「今わかっている研究の状況」を示すもので、効果を保証するものではありません。

( 01 )EVIDENCE / PUBMED · 5件

世界の論文

直近の研究を、やさしい日本語で

各論文の見出しにある「確からしさ」は、その研究がどれくらい信頼できるかの目安です。「理論段階」はまだ仮説に近く、下にいくほど多くの患者で検証されていて、「メタ解析」がもっとも信頼できます。

システマティックレビュー/メタ解析
MK-01 · PMID 42733672

自己免疫疾患に伴う血栓症:その仕組み、患者数、そして予防法

Autoimmune-associated thrombosis: mechanisms, population burden, and prevention strategies

Abstract / 原文

UNLABELLED: Autoimmune diseases, including systemic lupus erythematosus, rheumatoid arthritis, antiphospholipid syndrome, and systemic vasculitis, are associated with increased risk of thrombosis, accelerated atherosclerosis, cardiovascular-events, and premature mortality. Heparin-induced thrombocytopaenia and vaccine-induced thrombocytopaenia and thrombosis (VITT) or VITT like syndrome are autoimmune thrombotic disorders that do not have additional features of autoimmune diseases. We summarise the epidemiology, pathophysiology, diagnosis, and management of autoimmune thrombosis. Key mechanisms include autoantibody-mediated coagulation activation, endothelial dysfunction, complement activation, platelet activation, neutrophil extracellular-trap formation, and thrombo-inflammation, promoting thrombin generation, impaired fibrinolysis, and vascular injury. Traditional cardiovascular risk factors, such as smoking, obesity, hypertension, diabetes mellitus, and infection, further amplify thrombotic risk. Management requires integrated strategies combining anticoagulation, immunomodulatory therapy, cardiovascular-risk reduction, and long-term surveillance. Autoimmune thrombosis is an under-recognised contributor to cardiovascular disease and premature mortality across Europe. Earlier diagnosis, improved risk stratification, multidisciplinary care, and integration of autoimmune diseases into European cardiovascular prevention and health-system strategies are essential to reduce morbidity and premature mortality. FUNDING: DJA is funded by Medical Research Council UK (MR/Z505274/1) and infrastructure support was provided by the NIHR Imperial Biomedical Research Centre.

今の治療への意味自己免疫疾患と血栓症の関係について、これまでの研究をまとめたもので、血栓症のリスクが高いことを示唆しています。ただし、個々の患者さんへの直接的な治療法を示すものではありません。

この論文は、自己免疫疾患と血栓症の一般的な関係について解説したものです。ご自身の病状や治療については、必ず主治医にご相談ください。

Journal
The Lancet regional health. Europe(2026 Nov)
Authors
3名
Type
Journal Article, Review

複数の研究結果をまとめたレビュー論文です。

PubMedで原文を見る
観察研究
MK-02 · PMID 42732976

全身性エリテマトーデス(SLE)におけるCD4陽性T細胞のサブタイプ別CD73発現の変化と病気の活動性との関連

Redistribution of CD73 Expression on CD4+T Subpopulations in Systemic Lupus Erythematosus and Its Association With Disease Activity

Abstract / 原文

Systemic lupus erythematosus (SLE) is a complex autoimmune disorder driven by aberrant immune responses, predominately CD4 + T cells dysfunction. CD73, an ecto-5'-nucleotidase mediating adenosine signalling, is essential for immune regulation. Herein, we investigated CD73 expression across CD4 + T subpopulations and further explored their potential impacts on the activation and function of CD4 + T subsets, together with their associations with disease activity and clinical features of SLE. A total of 134 SLE patients, 84 disease controls antiphospholipid syndrome (APS), and 61 healthy controls (HCs) were recruited. Flow cytometry was used to profile CD73 expression across circulating CD4 + T subsets. Disease activity was assessed by SLEDAI-2 K score. We identified a subset-specific distribution pattern of CD73 expression in SLE compared with HCs, characterized by increased CD73 expression in Th1 and Th17 cells and reduced expression in Th2, Tregs, Tfh and Tfr cells. Meanwhile, significant elevated CD73-expressing Th1/Th2 ratios and obviously reduced CD73-expressing Tfh/Tfr ratios in SLE were observed. CD73-expressing Th1 cells exhibited enhanced activation phenotype manifested as elevated expression of CD25, ICOS, PD-1, and secretion of IFN-γ. Positive correlation was observed between CD73-expressing Th1 cells and CD25 expression within Th1 cells. In addition, CD73-expressing Tph cells displayed reduced secretion of IFN-γ and IL-21, and positive association was found between CD73 expression and IL-21 secretion within Tph cells. Importantly, frequencies of CD73-expressing Th1, Th2 and Tph cells were significantly reduced in active disease group relative to inactive group, and negatively correlated with SLEDAI-2 K scores, and CD73-expressing Th1 cells displayed moderate discriminatory capacity (AUC = 0.671) to differentiate active and inactive SLE. Furthermore, SLE patients with lupus nephritis showed decreased CD73-expressing Th1 cells and Tph cells, and Tph cells was diminished in patients with thrombocytopenia. These findings highlighted CD73 as a potential marker of immune dysregulation, which may be associated with the activation- and function-related cellular phenotypes. Aberrant CD73 expression may potentially be associated with disease activity and clinical manifestations of SLE patients.

今の治療への意味SLEの病気の活動性を評価する新しい指標になる可能性が示唆されていますが、現時点では直接的な治療法につながるものではありません。

この研究は、SLEの免疫細胞の変化について調べたものです。ご自身の病状の診断や治療方針については、必ず主治医にご相談ください。

Journal
Immunology(2026 Sep)
Authors
7名
Type
Journal Article

SLE患者さんと健常者を比較した観察研究です。

PubMedで原文を見る
システマティックレビュー/メタ解析
MK-03 · PMID 42731915

新生児期の抗リン脂質抗体症候群(APS)に伴う血栓症:診断の落とし穴と治療の最前線

Neonatal antiphospholipid syndrome-associated thrombosis: Diagnostic pitfalls and therapeutic frontiers

Abstract / 原文

Neonatal antiphospholipid syndrome (APS) is an exceptionally rare but clinically significant thrombotic disorder associated with antiphospholipid antibodies (aPL) in the neonatal period. Two principal pathogenic mechanisms have been proposed: passive transplacental transfer of maternal antiphospholipid antibodies and de novo neonatal production of aPL. Although approximately 30% of neonates born to aPL-positive mothers exhibit detectable antibodies at birth, thrombotic complications remain exceedingly uncommon. A "second-hit" model involving additional prothrombotic triggers such as infection, perinatal stress, inherited thrombophilia, or vascular catheters likely contributes to thrombogenesis. Available evidence from case reports and small series indicates that arterial thrombosis predominates, particularly neonatal arterial ischemic stroke, while venous thrombosis is less frequent. Diagnosis remains challenging because no validated neonatal-specific classification criteria exist, and interpretation of laboratory findings is confounded by transient maternal antibody transfer. Current diagnostic approaches rely on clinical suspicion, thrombosis confirmation, maternal antibody testing, serial neonatal aPL measurements, and exclusion of other prothrombotic conditions. Management strategies are extrapolated from pediatric and adult APS guidelines, with low-molecular-weight heparin representing the mainstay of anticoagulant therapy in affected neonates. Neonatal APS remains a diagnostic challenge due to its rarity and atypical presentations. Establishing age-specific criteria and long-term neurodevelopmental follow-up is critical for improving clinical outcomes and understanding the prognosis of this early-onset autoimmune condition. This narrative review aims to summarize current evidence regarding the pathophysiology, clinical manifestations, diagnostic challenges, and management of APS-associated thrombosis regarding the distinct neonatal population.

今の治療への意味新生児期のAPSの診断と治療の現状についてまとめられており、今後の診療に役立つ情報が含まれています。ただし、非常にまれな疾患のため、個々の患者さんへの直接的な治療法を示すものではありません。

この論文は、新生児期のAPSという非常にまれな病気について解説したものです。ご自身の病状や治療については、必ず主治医にご相談ください。

Journal
Blood reviews(2026 Sep)
Authors
10名
Type
Journal Article, Review

新生児期のAPSに関するこれまでの研究をまとめたレビュー論文です。

PubMedで原文を見る
症例報告
MK-04 · PMID 42730324

血栓性抗リン脂質抗体症候群(APS)発症に先行する、思春期発症の舞踏病の症例報告

Remote Adolescent-Onset Chorea Preceding Thrombotic Antiphospholipid Syndrome: A Case Report

Abstract / 原文

Antiphospholipid syndrome (APS) is a systemic autoimmune disease characterized by vascular thrombosis and/or obstetric morbidity in the presence of persistent antiphospholipid antibodies. Chorea is an uncommon neurological manifestation, reported in approximately 1% of patients, and is not included among the clinical domains required for classification. We report the case of a 28-year-old woman who presented with acute left-sided sensorimotor deficits. Her only relevant history was an episode of chorea involving the left upper limb at 18 years of age, which resolved spontaneously after an incomplete etiological workup at another institution. Neuroimaging demonstrated a right frontal ischemic lesion, and cardioembolic and large-vessel causes were excluded. Prompted by the prior history of chorea, testing revealed persistently high-titer anticardiolipin IgG and anti-β2-glycoprotein I IgG antibodies, establishing a diagnosis of primary APS. She was started on warfarin and achieved functional independence without recurrent vascular events. This case illustrates that juvenile-onset chorea may represent the heralding manifestation of APS, preceding the qualifying thrombotic event by a decade. An isolated, self-limited chorea of undetermined cause should prompt antiphospholipid antibody testing, as early recognition may allow timely thromboprophylaxis and potentially prevent cerebrovascular events in young patients.

今の治療への意味舞踏病がAPSの初期症状である可能性を示唆する一例ですが、非常にまれなケースです。APSの早期発見のヒントになるかもしれませんが、直接的な治療法を示すものではありません。

この論文は、特定の患者さんの経験を報告したものです。ご自身の病状や治療については、必ず主治医にご相談ください。

Journal
Cureus(2026 Aug)
Authors
3名
Type
Case Reports, Journal Article

特定の患者さんの詳細な経過を報告する症例報告です。

PubMedで原文を見る
症例報告
MK-05 · PMID 42729056

大動脈弁のライブマンサックス心内膜炎で、大動脈基部と冠動脈起始部への広がりを伴った症例報告

Aortic valve Libman-Sacks endocarditis with aortic root and coronary ostium involvement - A case report

Abstract / 原文

BACKGROUND: Libman-Sacks (LS) endocarditis, a nonbacterial thrombotic endocarditis, is the most frequent cardiac manifestation of systemic lupus erythematosus (SLE), particularly when associated with antiphospholipid syndrome (APS). It usually involves the mitral valve and is often clinically silent. CASE SUMMARY: We present a 25-year-old woman with SLE and APS who developed acute hemodynamic deterioration. Urgent surgery revealed a large endocarditic mass arising from the aortic valve leaflet, extending to the aortic root and obstructing the right coronary ostium. Resection and valve replacement were performed successfully. DISCUSSION: Unlike typical LS endocarditis, which manifests as mild valvular lesions, this case demonstrates rare aortic root involvement with coronary ostial obstruction. A review of the literature confirms that such an extension has not been previously reported, underscoring the heterogeneous and potentially life-threatening nature of LS endocarditis. TAKE HOME MESSAGES: LS endocarditis can present atypically. Recognition of unusual patterns is critical for timely intervention.

今の治療への意味ライブマンサックス心内膜炎のまれな病態を示しており、重症化する可能性もあることを示唆しています。診断や治療の参考になる可能性がありますが、個々の患者さんへの直接的な治療法を示すものではありません。

この論文は、特定の患者さんの経験を報告したものです。ご自身の病状や治療については、必ず主治医にご相談ください。

Journal
Frontiers in cardiovascular medicine(2026)
Authors
4名
Type
Case Reports, Journal Article

特定の患者さんの詳細な経過を報告する症例報告です。

PubMedで原文を見る
( 02 )TRIALS / JAPAN · 1件

日本で参加できる治験

現在 募集中のもの

各治験の「対象の目安」は年齢などの参加条件の一部です。ここに合っていても他の条件(病状・治療歴など)があります。詳しい参加条件は各治験ページで確認し、参加の可否は必ず主治医とご相談ください。

募集中
TR-01 · NCT06371417

免疫疾患に対するRAY121の第1b相試験(RAINBOW試験)

Phase 1b Trial of RAY121 in Immunological Diseases (RAINBOW Trial)

Phase
PHASE1
対象の目安
18歳〜85歳
Country
日本・Croatia・Turkey (Türkiye)・アメリカ・イタリア・オランダ・オーストラリア・オーストリア・カナダ・スペイン・チェコ・ドイツ・ノルウェー・ハンガリー・フランス・ブルガリア・ポルトガル・ポーランド・ルーマニア・台湾
詳細・参加条件を見る
( 03 )REGISTRY / jRCT

治験をもっと探す

日本の公式レジストリで全件を確認

上の一覧は ClinicalTrials.gov の一部です。日本国内の治験の多くは、日本の公式レジストリ jRCT にのみ登録されています。下記から最新の全件を確認できます。

jRCT で検索日本の臨床研究実施計画 公開システム「対象疾患名」に 原発性抗リン脂質抗体症候群 を入力し、「募集状況」で 募集中 にチェックして検索します。ClinicalTrials.gov で全件を見る世界最大の治験データベース(英語)「原発性抗リン脂質抗体症候群・日本・募集中」の条件で一覧が開きます。

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( 04 )SUPPORT

患者会・相談窓口

一人で抱え込まないでください

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